Victoria Gray underwent a gene editing experiment 4 years ago. Victoria had sickle cell. This CRISPR technique (gene editing) (Doctors removed some of her bone marrow cells, genetically modified them with CRISPR and infused billions of the modified cells back into her body. The genetic modification was designed to make the cells produce fetal hemoglobin, in the hopes the cells would compensate for the defective hemoglobin that causes the disease. [more of the story here and below]) is new. It is really the first therapy to truly treat Sickle Cell. This is truly exciting!!!
From NPR:
Victoria Gray was wandering through the British Museum in London last week when she spotted a small wooden cross hanging on the wall.
“It’s nice seeing all the old artifacts, especially the cross,” Gray said. “Religion is something that I hold close to my heart, and my faith is what brought me this far.”
Almost four years ago, Gray became one of the first patients with a genetic disorder — and the first patient with sickle cell disease — to get an experimental treatment that uses the revolutionary gene-editing technique known as CRISPR.
Wow